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Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study.
Rudnicki, Stacy A; Andrews, Jinsy A; Duong, Tina; Cockroft, Bettina M; Malik, Fady I; Meng, Lisa; Wei, Jenny; Wolff, Andrew A; Genge, Angela; Johnson, Nicholas E; Tesi-Rocha, Carolina; Connolly, Anne M; Darras, Basil T; Felice, Kevin; Finkel, Richard S; Shieh, Perry B; Mah, Jean K; Statland, Jeffrey; Campbell, Craig; Habib, Ali A; Kuntz, Nancy L; Oskoui, Maryam; Day, John W.
Afiliação
  • Rudnicki SA; Cytokinetics, Incorporated, South San Francisco, CA, USA.
  • Andrews JA; Cytokinetics, Incorporated, South San Francisco, CA, USA.
  • Duong T; Columbia University, New York, NY, USA.
  • Cockroft BM; Stanford University, Stanford, CA, USA.
  • Malik FI; Cytokinetics, Incorporated, South San Francisco, CA, USA.
  • Meng L; Sangamo Therapeutics, Brisbane, CA, USA.
  • Wei J; Cytokinetics, Incorporated, South San Francisco, CA, USA.
  • Wolff AA; Cytokinetics, Incorporated, South San Francisco, CA, USA.
  • Genge A; Cytokinetics, Incorporated, South San Francisco, CA, USA.
  • Johnson NE; Cytokinetics, Incorporated, South San Francisco, CA, USA.
  • Tesi-Rocha C; Montreal Neurological Institute, Montreal, QC, Canada.
  • Connolly AM; Virginia Commonwealth University, Richmond, VA, USA.
  • Darras BT; University of Utah, Salt Lake City, UT, USA.
  • Felice K; Stanford University, Stanford, CA, USA.
  • Finkel RS; Nationwide Children's Hospital, Columbus, OH, USA.
  • Shieh PB; Washington University, St Louis, MO, USA.
  • Mah JK; Boston Children's Hospital and Harvard Medical School, Boston, MA, USA.
  • Statland J; Hospital for Special Care, New Britain, CT, USA.
  • Campbell C; Nemours Children's Hospital, Orlando, FL, USA.
  • Habib AA; St. Jude Children's Research Hospital, Memphis, TN, USA.
  • Kuntz NL; University of California, Los Angeles, Los Angeles, CA, USA.
  • Oskoui M; University of Calgary, Alberta Children's Hospital, Calgary, AB, Canada.
  • Day JW; University of Kansas, Lawrence, KS, USA.
Neurotherapeutics ; 18(2): 1127-1136, 2021 04.
Article em En | MEDLINE | ID: mdl-33624184

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Piridinas / Pirimidinas / Pirróis / Atrofia Muscular Espinal / Drogas em Investigação / Músculo Esquelético / Troponina I Tipo de estudo: Clinical_trials / Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limite: Adolescent / Adult / Aged / Child / Female / Humans / Male / Middle aged Idioma: En Revista: Neurotherapeutics Assunto da revista: NEUROLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Piridinas / Pirimidinas / Pirróis / Atrofia Muscular Espinal / Drogas em Investigação / Músculo Esquelético / Troponina I Tipo de estudo: Clinical_trials / Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limite: Adolescent / Adult / Aged / Child / Female / Humans / Male / Middle aged Idioma: En Revista: Neurotherapeutics Assunto da revista: NEUROLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Estados Unidos