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Preclinical correction of human Fanconi anemia complementation group A bone marrow cells using a safety-modified lentiviral vector.
Becker, P S; Taylor, J A; Trobridge, G D; Zhao, X; Beard, B C; Chien, S; Adair, J; Kohn, D B; Wagner, J E; Shimamura, A; Kiem, H-P.
Affiliation
  • Becker PS; Division of Hematology, Department of Medicine, University of Washington, 815 Mercer Street, Seattle, WA 98109, USA. pbecker@u.washington.edu
Gene Ther ; 17(10): 1244-52, 2010 Oct.
Article in En | MEDLINE | ID: mdl-20485382

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Lentivirus / Fanconi Anemia Complementation Group A Protein / Fanconi Anemia Limits: Humans Language: En Journal: Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2010 Document type: Article Affiliation country:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Lentivirus / Fanconi Anemia Complementation Group A Protein / Fanconi Anemia Limits: Humans Language: En Journal: Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2010 Document type: Article Affiliation country: