Redirecting N-acetylaspartate metabolism in the central nervous system normalizes myelination and rescues Canavan disease.
JCI Insight
; 2(3): e90807, 2017 02 09.
Article
in En
| MEDLINE
| ID: mdl-28194442
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Genetic Therapy
/
Canavan Disease
/
Amidohydrolases
/
Genetic Vectors
Type of study:
Prognostic_studies
Limits:
Animals
/
Humans
Language:
En
Journal:
JCI Insight
Year:
2017
Document type:
Article
Country of publication: