The effect of galsulfase enzyme replacement therapy on the growth of patients with mucopolysaccharidosis VI (Maroteaux-Lamy syndrome).
Mol Genet Metab
; 122(1-2): 107-112, 2017 09.
Article
in En
| MEDLINE
| ID: mdl-28457718
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Body Height
/
Mucopolysaccharidosis VI
/
N-Acetylgalactosamine-4-Sulfatase
/
Enzyme Replacement Therapy
Type of study:
Observational_studies
/
Prognostic_studies
/
Risk_factors_studies
Limits:
Adolescent
/
Child
/
Child, preschool
/
Female
/
Humans
/
Infant
/
Male
/
Newborn
Language:
En
Journal:
Mol Genet Metab
Journal subject:
BIOLOGIA MOLECULAR
/
BIOQUIMICA
/
METABOLISMO
Year:
2017
Document type:
Article
Country of publication: