Differential Prevalence of Antibodies Against Adeno-Associated Virus in Healthy Children and Patients with Mucopolysaccharidosis III: Perspective for AAV-Mediated Gene Therapy.
Hum Gene Ther Clin Dev
; 28(4): 187-196, 2017 12.
Article
in En
| MEDLINE
| ID: mdl-29064732
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Genetic Therapy
/
Mucopolysaccharidosis III
/
Antibodies, Viral
Type of study:
Prevalence_studies
/
Risk_factors_studies
Limits:
Child
/
Humans
Language:
En
Journal:
Hum Gene Ther Clin Dev
Year:
2017
Document type:
Article
Country of publication: