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Differential Prevalence of Antibodies Against Adeno-Associated Virus in Healthy Children and Patients with Mucopolysaccharidosis III: Perspective for AAV-Mediated Gene Therapy.
Fu, Haiyan; Meadows, Aaron S; Pineda, Ricardo J; Kunkler, Krista L; Truxal, Kristen V; McBride, Kim L; Flanigan, Kevin M; McCarty, Douglas M.
Affiliation
  • Fu H; 1 Center for Gene Therapy, Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • Meadows AS; 4 Department of Pediatrics, School of Medicine The Ohio State University , Columbus, Ohio.
  • Pineda RJ; 1 Center for Gene Therapy, Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • Kunkler KL; 1 Center for Gene Therapy, Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • Truxal KV; 1 Center for Gene Therapy, Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • McBride KL; 1 Center for Gene Therapy, Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • Flanigan KM; 3 Division of Molecular and Human Genetics, Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • McCarty DM; 4 Department of Pediatrics, School of Medicine The Ohio State University , Columbus, Ohio.
Hum Gene Ther Clin Dev ; 28(4): 187-196, 2017 12.
Article in En | MEDLINE | ID: mdl-29064732

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Mucopolysaccharidosis III / Antibodies, Viral Type of study: Prevalence_studies / Risk_factors_studies Limits: Child / Humans Language: En Journal: Hum Gene Ther Clin Dev Year: 2017 Document type: Article Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Mucopolysaccharidosis III / Antibodies, Viral Type of study: Prevalence_studies / Risk_factors_studies Limits: Child / Humans Language: En Journal: Hum Gene Ther Clin Dev Year: 2017 Document type: Article Country of publication: