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Newborn Screening and Emerging Therapies for X-Linked Adrenoleukodystrophy.
Moser, Ann B; Fatemi, Ali.
Affiliation
  • Moser AB; Kennedy Krieger Institute, Baltimore, Maryland.
  • Fatemi A; Kennedy Krieger Institute, Baltimore, Maryland.
JAMA Neurol ; 75(10): 1175-1176, 2018 10 01.
Article in En | MEDLINE | ID: mdl-29946687

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Neonatal Screening / Adrenoleukodystrophy Type of study: Diagnostic_studies / Prognostic_studies / Screening_studies Limits: Humans / Male / Newborn Language: En Journal: JAMA Neurol Year: 2018 Document type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Neonatal Screening / Adrenoleukodystrophy Type of study: Diagnostic_studies / Prognostic_studies / Screening_studies Limits: Humans / Male / Newborn Language: En Journal: JAMA Neurol Year: 2018 Document type: Article