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Tailoring the AAV2 capsid vector for bone-targeting.
Alméciga-Díaz, Carlos J; Montaño, Adriana M; Barrera, Luis A; Tomatsu, Shunji.
Affiliation
  • Alméciga-Díaz CJ; Institute for the Study of Inborn Errors of Metabolism, Pontificia Universidad Javeriana, Bogotá, DC, Colombia. cjalmeciga@javeriana.edu.co.
  • Montaño AM; Department of Pediatrics, School of Medicine, Saint Louis University, St. Louis, MO, USA. adriana.montano@health.slu.edu.
  • Barrera LA; Institute for the Study of Inborn Errors of Metabolism, Pontificia Universidad Javeriana, Bogotá, DC, Colombia.
  • Tomatsu S; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA. shunji.tomatsu@nemours.org.
Pediatr Res ; 84(4): 545-551, 2018 10.
Article in En | MEDLINE | ID: mdl-30323349

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Bone and Bones / Mucopolysaccharidosis IV / Durapatite / Capsid Proteins / Genetic Vectors Limits: Animals / Humans Language: En Journal: Pediatr Res Year: 2018 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Bone and Bones / Mucopolysaccharidosis IV / Durapatite / Capsid Proteins / Genetic Vectors Limits: Animals / Humans Language: En Journal: Pediatr Res Year: 2018 Document type: Article Affiliation country: Country of publication: