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Gene therapy targeting SARM1 blocks pathological axon degeneration in mice.
Geisler, Stefanie; Huang, Shay X; Strickland, Amy; Doan, Ryan A; Summers, Daniel W; Mao, Xianrong; Park, Jiwoong; DiAntonio, Aaron; Milbrandt, Jeffrey.
Affiliation
  • Geisler S; Department of Neurology, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • Huang SX; Hope Center for Neurological Disorders, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • Strickland A; Department of Neurology, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • Doan RA; Department of Genetics, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • Summers DW; Department of Neurology, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • Mao X; Department of Genetics, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • Park J; Department of Genetics, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • DiAntonio A; Department of Genetics, Washington University School of Medicine in St. Louis, St. Louis, MO.
  • Milbrandt J; Department of Developmental Biology, Washington University School of Medicine in St. Louis, St. Louis, MO diantonio@wustl.edu.
J Exp Med ; 216(2): 294-303, 2019 02 04.
Article in En | MEDLINE | ID: mdl-30642945

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Axons / Genetic Therapy / Dependovirus / Gene Targeting / Cytoskeletal Proteins / Armadillo Domain Proteins / Nerve Degeneration Limits: Animals / Humans Language: En Journal: J Exp Med Year: 2019 Document type: Article Affiliation country:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Axons / Genetic Therapy / Dependovirus / Gene Targeting / Cytoskeletal Proteins / Armadillo Domain Proteins / Nerve Degeneration Limits: Animals / Humans Language: En Journal: J Exp Med Year: 2019 Document type: Article Affiliation country: