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High level of fetal-globin reactivation by designed transcriptional activator-like effector.
Zhan, Jun; Irudayam, Maria Johnson; Nakamura, Yukio; Kurita, Ryo; Nienhuis, Arthur W.
Affiliation
  • Zhan J; Division of Experimental Hematology, Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN.
  • Irudayam MJ; Division of Experimental Hematology, Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN.
  • Nakamura Y; Cell Engineering Division, RIKEN BioResource Research Center, National Research and Development Agency, University of Tsukuba, Tsukuba, Japan; and.
  • Kurita R; Department of Research and Development, Central Blood Institute, Japanese Red Cross Society, Tokyo, Japan.
  • Nienhuis AW; Division of Experimental Hematology, Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN.
Blood Adv ; 4(4): 687-695, 2020 02 25.
Article in En | MEDLINE | ID: mdl-32084259

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Gamma-Globins / Transcription Activator-Like Effectors Limits: Adult / Humans Language: En Journal: Blood Adv Year: 2020 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Gamma-Globins / Transcription Activator-Like Effectors Limits: Adult / Humans Language: En Journal: Blood Adv Year: 2020 Document type: Article Affiliation country: Country of publication: