Your browser doesn't support javascript.
loading
Krabbe disease successfully treated via monotherapy of intrathecal gene therapy.
Bradbury, Allison M; Bagel, Jessica H; Nguyen, Duc; Lykken, Erik A; Pesayco Salvador, Jill; Jiang, Xuntian; Swain, Gary P; Assenmacher, Charles A; Hendricks, Ian J; Miyadera, Keiko; Hess, Rebecka S; Ostrager, Arielle; ODonnell, Patricia; Sands, Mark S; Ory, Daniel S; Shelton, G Diane; Bongarzone, Ernesto R; Gray, Steven J; Vite, Charles H.
Affiliation
  • Bradbury AM; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Bagel JH; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Nguyen D; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, Illinois, USA.
  • Lykken EA; Department of Pediatrics, University of Texas Southwestern Medical Center, Dallas, Texas, USA.
  • Pesayco Salvador J; Department of Pathology, School of Medicine, University of California San Diego, La Jolla, California, USA.
  • Jiang X; Department of Medicine, Washington University School of Medicine, St. Louis, Missouri, USA.
  • Swain GP; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Assenmacher CA; Department of Pathobiology, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Hendricks IJ; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Miyadera K; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Hess RS; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Ostrager A; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • ODonnell P; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
  • Sands MS; Department of Medicine, Washington University School of Medicine, St. Louis, Missouri, USA.
  • Ory DS; Department of Medicine, Washington University School of Medicine, St. Louis, Missouri, USA.
  • Shelton GD; Department of Pathology, School of Medicine, University of California San Diego, La Jolla, California, USA.
  • Bongarzone ER; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, Illinois, USA.
  • Gray SJ; Department of Pediatrics, University of Texas Southwestern Medical Center, Dallas, Texas, USA.
  • Vite CH; Department of Clinical Sciences and Advanced Medicine, School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA.
J Clin Invest ; 130(9): 4906-4920, 2020 09 01.
Article in En | MEDLINE | ID: mdl-32773406
Subject(s)
Key words
Fulltext
Add to My VHL
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Dependovirus / Galactosylceramidase / Leukodystrophy, Globoid Cell Type of study: Prognostic_studies Limits: Animals Language: En Journal: J Clin Invest Year: 2020 Document type: Article Affiliation country: Country of publication:
Fulltext
Add to My VHL
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Dependovirus / Galactosylceramidase / Leukodystrophy, Globoid Cell Type of study: Prognostic_studies Limits: Animals Language: En Journal: J Clin Invest Year: 2020 Document type: Article Affiliation country: Country of publication: