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Modulators of CFTR. Updates on clinical development and future directions.
Bardin, Emmanuelle; Pastor, Alexandra; Semeraro, Michaela; Golec, Anita; Hayes, Kate; Chevalier, Benoit; Berhal, Farouk; Prestat, Guillaume; Hinzpeter, Alexandre; Gravier-Pelletier, Christine; Pranke, Iwona; Sermet-Gaudelus, Isabelle.
Affiliation
  • Bardin E; Institut Necker Enfants Malades. INSERM U1151, Paris, France.
  • Pastor A; LCBPT, UMR CNRS 8601, Paris, France; Université de Paris, Paris, France.
  • Semeraro M; Centre d'Investigation Clinique, Unité de Recherche Clinique-CIC P1419, Hôpital Necker Enfants Malades, Université de Paris, Paris, France.
  • Golec A; Institut Necker Enfants Malades. INSERM U1151, Paris, France.
  • Hayes K; Clinical Trial Network, European Cystic Fibrosis Society, Belfast, Ireland.
  • Chevalier B; Institut Necker Enfants Malades. INSERM U1151, Paris, France.
  • Berhal F; LCBPT, UMR CNRS 8601, Paris, France; Université de Paris, Paris, France.
  • Prestat G; LCBPT, UMR CNRS 8601, Paris, France; Université de Paris, Paris, France.
  • Hinzpeter A; Institut Necker Enfants Malades. INSERM U1151, Paris, France.
  • Gravier-Pelletier C; LCBPT, UMR CNRS 8601, Paris, France; Université de Paris, Paris, France.
  • Pranke I; Institut Necker Enfants Malades. INSERM U1151, Paris, France.
  • Sermet-Gaudelus I; Institut Necker Enfants Malades. INSERM U1151, Paris, France; Université de Paris, Paris, France; Clinical Trial Network, European Cystic Fibrosis Society, Belfast, Ireland; Centre de Référence Maladies Rares, Mucoviscidose et Maladies de CFTR, Hôpital Necker Enfants Malades, Paris, France; European
Eur J Med Chem ; 213: 113195, 2021 Mar 05.
Article in En | MEDLINE | ID: mdl-33524685

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Quinolones / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Benzodioxoles / Drug Development / Aminophenols / Aminopyridines / Indoles Type of study: Diagnostic_studies / Prognostic_studies Limits: Humans Language: En Journal: Eur J Med Chem Year: 2021 Document type: Article Affiliation country:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Quinolones / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Benzodioxoles / Drug Development / Aminophenols / Aminopyridines / Indoles Type of study: Diagnostic_studies / Prognostic_studies Limits: Humans Language: En Journal: Eur J Med Chem Year: 2021 Document type: Article Affiliation country: