Nusinersen treatment in adults with severe spinal muscular atrophy: A real-life retrospective observational cohort study.
Rev Neurol (Paris)
; 178(3): 234-240, 2022 Mar.
Article
in En
| MEDLINE
| ID: mdl-35000792
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Muscular Atrophy, Spinal
/
Spinal Muscular Atrophies of Childhood
/
Neurodegenerative Diseases
Type of study:
Etiology_studies
/
Observational_studies
/
Prognostic_studies
Limits:
Adult
/
Humans
Country/Region as subject:
America do norte
Language:
En
Journal:
Rev Neurol (Paris)
Year:
2022
Document type:
Article
Country of publication: