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Biodistribution of Adeno-Associated Virus Gene Therapy Following Cerebrospinal Fluid-Directed Administration.
Chen, Xin; Lim, Daniel A; Lawlor, Michael W; Dimmock, David; Vite, Charles H; Lester, Thomas; Tavakkoli, Fatemeh; Sadhu, Chanchal; Prasad, Suyash; Gray, Steven J.
Affiliation
  • Chen X; Department of Pediatrics, University of Texas Southwestern Medical Center, Dallas, Texas, USA.
  • Lim DA; Department of Neurological Surgery, Eli and Edythe Broad Center for Regeneration Medicine, and the Weill Institute for Neurosciences, University of California San Francisco School of Medicine, San Francisco, California, USA.
  • Lawlor MW; Medical College of Wisconsin and Diverge Translational Science Laboratory, Milwaukee, Wisconsin, USA.
  • Dimmock D; Rady Children's Institute for Genomic Medicine, San Diego, California, USA.
  • Vite CH; School of Veterinary Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, USA; and.
  • Lester T; Taysha Gene Therapies, Dallas, Texas, USA.
  • Tavakkoli F; Taysha Gene Therapies, Dallas, Texas, USA.
  • Sadhu C; Taysha Gene Therapies, Dallas, Texas, USA.
  • Prasad S; Taysha Gene Therapies, Dallas, Texas, USA.
  • Gray SJ; Department of Pediatrics, University of Texas Southwestern Medical Center, Dallas, Texas, USA.
Hum Gene Ther ; 34(3-4): 94-111, 2023 02.
Article in En | MEDLINE | ID: mdl-36606687

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Dependovirus Type of study: Prognostic_studies / Risk_factors_studies Limits: Animals / Humans Language: En Journal: Hum Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2023 Document type: Article Affiliation country: Country of publication:

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Dependovirus Type of study: Prognostic_studies / Risk_factors_studies Limits: Animals / Humans Language: En Journal: Hum Gene Ther Journal subject: GENETICA MEDICA / TERAPEUTICA Year: 2023 Document type: Article Affiliation country: Country of publication: