Extraneuronal pathology in a canine model of CLN2 neuronal ceroid lipofuscinosis after intracerebroventricular gene therapy that delays neurological disease progression.
Gene Ther
; 24(4): 215-223, 2017 04.
Article
in En
| MEDLINE
| ID: mdl-28079862
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Genetic Therapy
/
Lysosomal Storage Diseases
/
Dipeptidyl-Peptidases and Tripeptidyl-Peptidases
/
Serine Proteases
/
Aminopeptidases
/
Neuronal Ceroid-Lipofuscinoses
Limits:
Animals
/
Humans
Language:
En
Journal:
Gene Ther
Journal subject:
GENETICA MEDICA
/
TERAPEUTICA
Year:
2017
Document type:
Article
Affiliation country:
Estados Unidos