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Insight into health-related quality of life of young children with haemophilia B treated with long-acting nonacog beta pegol recombinant factor IX.
Carcao, M; Kearney, S; Santagostino, E; Oyesiku, J O O; Young, N L; Meunier, J; Hoxer, C S; Zhang, C; Blanchette, V S.
Affiliation
  • Carcao M; Division of Haematology/Oncology, Department of Paediatrics, Child Health Evaluative Sciences, Research Institute, Hospital for Sick Children, University of Toronto, Toronto, ON, Canada.
  • Kearney S; CHCMN Hemophilia and Thrombosis Center Children's Hospital and Clinics of Minnesota, Minneapolis, MN, USA.
  • Santagostino E; Angelo Bianchi Bonomi Hemophilia and Thrombosis Centre, Istituto di Ricovero e Cura a Carattere Scientifico Cà Granda Foundation, Maggiore Hospital Policlinico, Milan, Italy.
  • Oyesiku JOO; Department of Haemophilia, Haemostasis and Thrombosis, Hampshire Hospitals NHS Foundation Trust, Basingstoke, Hampshire, UK.
  • Young NL; School of Rural and Northern Health and ECHO Research Centre, Laurentian University, Sudbury, ON, Canada.
  • Meunier J; Mapi, Patient-Centered Outcomes, Lyon, France.
  • Hoxer CS; Novo Nordisk A/S, Søborg, Denmark.
  • Zhang C; Division of Haematology/Oncology, Department of Paediatrics, Child Health Evaluative Sciences, Research Institute, Hospital for Sick Children, University of Toronto, Toronto, ON, Canada.
  • Blanchette VS; Division of Haematology/Oncology, Department of Paediatrics, Child Health Evaluative Sciences, Research Institute, Hospital for Sick Children, University of Toronto, Toronto, ON, Canada.
Haemophilia ; 23(3): e222-e224, 2017 05.
Article in En | MEDLINE | ID: mdl-28371032

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Polyethylene Glycols / Quality of Life / Factor IX / Hemophilia B Type of study: Clinical_trials Aspects: Patient_preference Limits: Child / Child, preschool / Female / Humans / Male Language: En Journal: Haemophilia Journal subject: HEMATOLOGIA Year: 2017 Document type: Article Affiliation country: Canadá Country of publication: Reino Unido

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Polyethylene Glycols / Quality of Life / Factor IX / Hemophilia B Type of study: Clinical_trials Aspects: Patient_preference Limits: Child / Child, preschool / Female / Humans / Male Language: En Journal: Haemophilia Journal subject: HEMATOLOGIA Year: 2017 Document type: Article Affiliation country: Canadá Country of publication: Reino Unido