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Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of ß-Hemoglobinopathies.
Bhukhai, Kanit; de Dreuzy, Edouard; Giorgi, Marie; Colomb, Charlotte; Negre, Olivier; Denaro, Maria; Gillet-Legrand, Béatrix; Cheuzeville, Joëlle; Paulard, Anaïs; Trebeden-Negre, Hélène; Borwornpinyo, Suparerk; Sii-Felice, Karine; Maouche, Leila; Down, Julian D; Leboulch, Phillippe; Payen, Emmanuel.
Affiliation
  • Bhukhai K; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France.
  • de Dreuzy E; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France.
  • Giorgi M; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France.
  • Colomb C; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France.
  • Negre O; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France; bluebird bio, Inc., Cambridge, MA 02141, USA; bluebird bio France, Fontenay aux Roses 92260, France.
  • Denaro M; bluebird bio, Inc., Cambridge, MA 02141, USA.
  • Gillet-Legrand B; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France; bluebird bio France, Fontenay aux Roses 92260, France.
  • Cheuzeville J; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France; bluebird bio France, Fontenay aux Roses 92260, France.
  • Paulard A; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France; bluebird bio France, Fontenay aux Roses 92260, France.
  • Trebeden-Negre H; Cell Therapy Unit, Pitie-Salpetriere Hospital, Paris 75013, France.
  • Borwornpinyo S; Mahidol University, Bangkok 10400, Thailand.
  • Sii-Felice K; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France.
  • Maouche L; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France; INSERM, Paris 75013, France.
  • Down JD; Institute for Medical Engineering and Science, Massachusetts Institute of Technology, Cambridge, MA 02139, USA.
  • Leboulch P; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France; Ramathibodi Hospital, Bangkok 10400, Thailand; Harvard Medical School and Genetics Division, Department of Medicine, Brigham & Women's Hospit
  • Payen E; CEA, Institute of Biology François Jacob, Fontenay aux Roses 92260, France; UMR_007, CEA and University of Paris Saclay, Fontenay aux Roses 92260, France; INSERM, Paris 75013, France. Electronic address: emmanuel.payen@cea.fr.
Mol Ther ; 26(2): 480-495, 2018 02 07.
Article in En | MEDLINE | ID: mdl-29221807

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Transduction, Genetic / Hematopoietic Stem Cells / Genetic Therapy / Hematopoietic Stem Cell Transplantation / Beta-Globins / Hemoglobinopathies Limits: Animals / Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2018 Document type: Article Affiliation country: Francia Country of publication: Estados Unidos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Transduction, Genetic / Hematopoietic Stem Cells / Genetic Therapy / Hematopoietic Stem Cell Transplantation / Beta-Globins / Hemoglobinopathies Limits: Animals / Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2018 Document type: Article Affiliation country: Francia Country of publication: Estados Unidos