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Reduction in Brain Heparan Sulfate with Systemic Administration of an IgG Trojan Horse-Sulfamidase Fusion Protein in the Mucopolysaccharidosis Type IIIA Mouse.
Boado, Ruben J; Lu, Jeff Zhiqiang; Hui, Eric Ka-Wai; Pardridge, William M.
Affiliation
  • Boado RJ; ArmaGen, Inc. , Calabasas, California 91302, United States.
  • Lu JZ; ArmaGen, Inc. , Calabasas, California 91302, United States.
  • Hui EK; ArmaGen, Inc. , Calabasas, California 91302, United States.
  • Pardridge WM; ArmaGen, Inc. , Calabasas, California 91302, United States.
Mol Pharm ; 15(2): 602-608, 2018 02 05.
Article in En | MEDLINE | ID: mdl-29251941

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Brain / Immunoglobulin G / Mucopolysaccharidosis III / Heparitin Sulfate / Hydrolases Limits: Animals / Female / Humans / Male Language: En Journal: Mol Pharm Journal subject: BIOLOGIA MOLECULAR / FARMACIA / FARMACOLOGIA Year: 2018 Document type: Article Affiliation country: Estados Unidos Country of publication: Estados Unidos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Brain / Immunoglobulin G / Mucopolysaccharidosis III / Heparitin Sulfate / Hydrolases Limits: Animals / Female / Humans / Male Language: En Journal: Mol Pharm Journal subject: BIOLOGIA MOLECULAR / FARMACIA / FARMACOLOGIA Year: 2018 Document type: Article Affiliation country: Estados Unidos Country of publication: Estados Unidos