Your browser doesn't support javascript.
loading
Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice.
Song, Chunjuan; Conlon, Thomas J; Deng, Wen-Tao; Coleman, Kirsten E; Zhu, Ping; Plummer, Cayrn; Mandapati, Savitri; Van Hoosear, Mailin; Green, Kari B; Sonnentag, Peter; Sharma, Alok K; Timmers, Adrian; Robinson, Paulette M; Knop, David R; Hauswirth, William W; Chulay, Jeffrey D; Shearman, Mark S; Ye, Guo-Jie.
Affiliation
  • Song C; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Conlon TJ; 2 CR Scientific and Compliance Consulting LLC, Gainesville, FL.
  • Deng WT; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Coleman KE; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Zhu P; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Plummer C; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Mandapati S; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Van Hoosear M; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Green KB; 4 Department of Chemistry, University of Florida, Gainesville, FL.
  • Sonnentag P; 5 Covance Inc, Madison, WI.
  • Sharma AK; 5 Covance Inc, Madison, WI.
  • Timmers A; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Robinson PM; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Knop DR; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Hauswirth WW; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Chulay JD; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Shearman MS; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Ye GJ; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
Hum Gene Ther Clin Dev ; 29(4): 188-197, 2018 12.
Article in En | MEDLINE | ID: mdl-30280954

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Carrier Proteins / Retinitis Pigmentosa / Dependovirus / G-Protein-Coupled Receptor Kinase 1 / Eye Proteins Type of study: Evaluation_studies Limits: Animals Language: En Journal: Hum Gene Ther Clin Dev Year: 2018 Document type: Article Country of publication: Estados Unidos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Carrier Proteins / Retinitis Pigmentosa / Dependovirus / G-Protein-Coupled Receptor Kinase 1 / Eye Proteins Type of study: Evaluation_studies Limits: Animals Language: En Journal: Hum Gene Ther Clin Dev Year: 2018 Document type: Article Country of publication: Estados Unidos