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Perspectives on Spinraza (Nusinersen) Treatment Study: Views of Individuals and Parents of Children Diagnosed with Spinal Muscular Atrophy.
Pacione, Michelle; Siskind, Carly E; Day, John W; Tabor, Holly K.
Affiliation
  • Pacione M; Department of Genetics, Stanford University School of Medicine, Stanford, California, USA.
  • Siskind CE; Department of Neurology and Neurological Sciences, Stanford Medicine, Stanford, California, USA.
  • Day JW; Department of Neurology and Neurological Sciences, Stanford Medicine, Stanford, California, USA.
  • Tabor HK; Department of Medicine, Stanford Center for Biomedical Ethics, Stanford University, Stanford, California, USA.
J Neuromuscul Dis ; 6(1): 119-131, 2019.
Article in En | MEDLINE | ID: mdl-30594933

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oligonucleotides / Muscular Atrophy, Spinal Type of study: Diagnostic_studies / Etiology_studies / Prognostic_studies / Qualitative_research Aspects: Patient_preference Limits: Adult / Female / Humans / Male / Middle aged Language: En Journal: J Neuromuscul Dis Year: 2019 Document type: Article Affiliation country: Estados Unidos Country of publication: Países Bajos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Oligonucleotides / Muscular Atrophy, Spinal Type of study: Diagnostic_studies / Etiology_studies / Prognostic_studies / Qualitative_research Aspects: Patient_preference Limits: Adult / Female / Humans / Male / Middle aged Language: En Journal: J Neuromuscul Dis Year: 2019 Document type: Article Affiliation country: Estados Unidos Country of publication: Países Bajos