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Predictive factors for lumacaftor/ivacaftor clinical response.
Masson, Alexandra; Schneider-Futschik, Elena K; Baatallah, Nesrine; Nguyen-Khoa, Thao; Girodon, Emmanuelle; Hatton, Aurélie; Flament, Thomas; Le Bourgeois, Muriel; Chedevergne, Frederique; Bailly, Céline; Kyrilli, Sylvia; Achimastos, Diane; Hinzpeter, Alexandre; Edelman, Aleksander; Sermet-Gaudelus, Isabelle.
Affiliation
  • Masson A; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France; Centre de Référence et de Compétence de la Mucoviscidose, Hôpital Dupuytren, 8 avenue Dominique Larrey, 87042 Limoges, France.
  • Schneider-Futschik EK; Drug Delivery, Disposition and Dynamics, Monash Institute of Pharmacy and Pharmaceutical Sciences, Monash University, Parkville, Victoria 3052, Australia; Lung Health Research Center, Department of Pharmacology & Therapeutics, School of Biomedical Sciences, Faculty of Medicine, Dentistry and Hea
  • Baatallah N; Institut Necker-Enfants Malades, INSERM U1151, 149 rue de Sèvres, 75015 Paris, France. Electronic address: nesrine.baatallah@inserm.fr.
  • Nguyen-Khoa T; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France; Institut Necker-Enfants Malades, INSERM U1151, 149 rue de Sèvres, 75015 Paris, France; Laboratoire de Biochimie Générale, Hôpital Necker-Enfants Malades,
  • Girodon E; Institut Necker-Enfants Malades, INSERM U1151, 149 rue de Sèvres, 75015 Paris, France; Service de Biochimie et Génétique Moléculaire, Hôpital Cochin, Assistance-Publique Hôpitaux de Paris, 27 rue du Faubourg Saint-Jacques, 75014 Paris, France. Electronic address: emmanuelle.girodon@aphp.fr.
  • Hatton A; Institut Necker-Enfants Malades, INSERM U1151, 149 rue de Sèvres, 75015 Paris, France. Electronic address: aurelie.hatton@inserm.fr.
  • Flament T; Centre de Ressources et de Compétence de la Mucoviscidose Adulte, Hôpital Bretonneau, Centre Hospitalier Régional Universitaire, 2 boulevard Tonnellé, 37000 Tours, France. Electronic address: t.flament@chu-tours.fr.
  • Le Bourgeois M; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France. Electronic address: muriel.lebourgeois@aphp.fr.
  • Chedevergne F; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France. Electronic address: frederique.chedevergne@aphp.fr.
  • Bailly C; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France. Electronic address: celine.bailly@aphp.fr.
  • Kyrilli S; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France.
  • Achimastos D; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France. Electronic address: diane.achimastos@aphp.fr.
  • Hinzpeter A; Institut Necker-Enfants Malades, INSERM U1151, 149 rue de Sèvres, 75015 Paris, France. Electronic address: alexandre.hinzpeter@inserm.fr.
  • Edelman A; Institut Necker-Enfants Malades, INSERM U1151, 149 rue de Sèvres, 75015 Paris, France. Electronic address: aleksander.edelman@inserm.fr.
  • Sermet-Gaudelus I; Centre Maladie Rare Mucoviscidose, Hôpital Necker-Enfants Malades, Assistance-Publique Hôpitaux de Paris, 149 rue de sèvres, 75015 Paris, France; Institut Necker-Enfants Malades, INSERM U1151, 149 rue de Sèvres, 75015 Paris, France; Université Paris Sorbonne, 75005 Paris, France. Electronic address:
J Cyst Fibros ; 18(3): 368-374, 2019 05.
Article in En | MEDLINE | ID: mdl-30595473

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Sweat / Drug Monitoring / Quinolones / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Benzodioxoles / Aminophenols / Aminopyridines Type of study: Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Language: En Journal: J Cyst Fibros Year: 2019 Document type: Article Affiliation country: Francia Country of publication: Países Bajos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Sweat / Drug Monitoring / Quinolones / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Benzodioxoles / Aminophenols / Aminopyridines Type of study: Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Language: En Journal: J Cyst Fibros Year: 2019 Document type: Article Affiliation country: Francia Country of publication: Países Bajos