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Human AlphoidtetO Artificial Chromosome as a Gene Therapy Vector for the Developing Hemophilia A Model in Mice.
Ponomartsev, Sergey V; Sinenko, Sergey A; Skvortsova, Elena V; Liskovykh, Mikhail A; Voropaev, Ivan N; Savina, Maria M; Kuzmin, Andrey A; Kuzmina, Elena Yu; Kondrashkina, Alexandra M; Larionov, Vladimir; Kouprina, Natalay; Tomilin, Alexey N.
Affiliation
  • Ponomartsev SV; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Sinenko SA; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Skvortsova EV; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Liskovykh MA; Developmental Therapeutics Branch, National Cancer Institute, Bethesda, MD 20892, USA.
  • Voropaev IN; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Savina MM; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Kuzmin AA; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Kuzmina EY; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Kondrashkina AM; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
  • Larionov V; Developmental Therapeutics Branch, National Cancer Institute, Bethesda, MD 20892, USA.
  • Kouprina N; Developmental Therapeutics Branch, National Cancer Institute, Bethesda, MD 20892, USA.
  • Tomilin AN; Institute of Cytology, Russian Academy of Sciences, 4 Tikhoretsky Ave., St-Petersburg 194064, Russia.
Cells ; 9(4)2020 04 03.
Article in En | MEDLINE | ID: mdl-32260189

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Chromosomes, Artificial, Human / Genetic Vectors / Hemophilia A Type of study: Prognostic_studies Limits: Animals / Humans Language: En Journal: Cells Year: 2020 Document type: Article Affiliation country: Rusia Country of publication: Suiza

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Chromosomes, Artificial, Human / Genetic Vectors / Hemophilia A Type of study: Prognostic_studies Limits: Animals / Humans Language: En Journal: Cells Year: 2020 Document type: Article Affiliation country: Rusia Country of publication: Suiza