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miR-143 Regulates Lysosomal Enzyme Transport across the Blood-Brain Barrier and Transforms CNS Treatment for Mucopolysaccharidosis Type I.
Lin, Yi; Wang, Xiaohong; Rose, Kevin P; Dai, Mei; Han, Jingfen; Xin, Mei; Pan, Dao.
Affiliation
  • Lin Y; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45219, USA.
  • Wang X; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45219, USA.
  • Rose KP; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45219, USA.
  • Dai M; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45219, USA.
  • Han J; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45219, USA.
  • Xin M; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45219, USA; Department of Pediatrics, University of Cincinnati, Cincinnati, OH 45229, USA.
  • Pan D; Division of Experimental Hematology and Cancer Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH 45219, USA; Department of Pediatrics, University of Cincinnati, Cincinnati, OH 45229, USA. Electronic address: dao.pan@cchmc.org.
Mol Ther ; 28(10): 2161-2176, 2020 10 07.
Article in En | MEDLINE | ID: mdl-32610100

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Blood-Brain Barrier / Central Nervous System / Mucopolysaccharidosis I / MicroRNAs / Lysosomes Limits: Animals / Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2020 Document type: Article Affiliation country: Estados Unidos Country of publication: Estados Unidos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Blood-Brain Barrier / Central Nervous System / Mucopolysaccharidosis I / MicroRNAs / Lysosomes Limits: Animals / Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2020 Document type: Article Affiliation country: Estados Unidos Country of publication: Estados Unidos