BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression.
Blood
; 137(6): 763-774, 2021 02 11.
Article
in En
| MEDLINE
| ID: mdl-33067633
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Recombinant Fusion Proteins
/
Factor IX
/
Genetic Therapy
/
Gene Expression Regulation
/
Hemophilia B
/
CpG Islands
Type of study:
Clinical_trials
/
Etiology_studies
/
Observational_studies
/
Risk_factors_studies
Limits:
Adolescent
/
Adult
/
Aged
/
Humans
/
Male
/
Middle aged
Language:
En
Journal:
Blood
Year:
2021
Document type:
Article