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Considerations for Systemic Use of Gene Therapy.
Byrne, Barry J; Corti, Manuela; Muntoni, Francesco.
Affiliation
  • Byrne BJ; Powell Gene Therapy Center and Child Health Research Institute, Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL, USA. Electronic address: barry.byrne@ufl.edu.
  • Corti M; Powell Gene Therapy Center and Child Health Research Institute, Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL, USA.
  • Muntoni F; Dubowitz Neuromuscular Centre, University College London, Great Ormond Street Institute of Child Health, London, UK; National Institute for Health Research Great Ormond Street Hospital Biomedical Research Centre, London, UK.
Mol Ther ; 29(2): 422-423, 2021 02 03.
Article in En | MEDLINE | ID: mdl-33485465

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Genetic Diseases, Inborn Limits: Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2021 Document type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Genetic Diseases, Inborn Limits: Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2021 Document type: Article