Your browser doesn't support javascript.
loading
Waning efficacy in a long-term AAV-mediated gene therapy study in the murine model of Krabbe disease.
Heller, Gregory J; Marshall, Michael S; Issa, Yazan; Marshall, Jeffrey N; Nguyen, Duc; Rue, Emily; Pathmasiri, Koralege C; Domowicz, Miriam S; van Breemen, Richard B; Tai, Leon M; Cologna, Stephanie M; Crocker, Stephen J; Givogri, Maria I; Sands, Mark S; Bongarzone, Ernesto R.
Affiliation
  • Heller GJ; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA.
  • Marshall MS; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA. Electronic address: mmarshall@mgh.harvard.edu.
  • Issa Y; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA.
  • Marshall JN; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA.
  • Nguyen D; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA.
  • Rue E; Linus Pauling Institute, Oregon State University, Corvallis, OR 97331, USA.
  • Pathmasiri KC; Department of Chemistry, University of Illinois at Chicago, Chicago, IL 60607, USA.
  • Domowicz MS; Department of Pediatrics, University of Chicago, Chicago, IL 60612, USA.
  • van Breemen RB; Linus Pauling Institute, Oregon State University, Corvallis, OR 97331, USA.
  • Tai LM; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA.
  • Cologna SM; Department of Chemistry, University of Illinois at Chicago, Chicago, IL 60607, USA.
  • Crocker SJ; Department of Neuroscience, University of Connecticut School of Medicine, Farmington, CT 06030, USA.
  • Givogri MI; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA.
  • Sands MS; Department of Medicine, Washington University in St. Louis, St. Louis, MO 63110, USA.
  • Bongarzone ER; Department of Anatomy and Cell Biology, College of Medicine, University of Illinois at Chicago, Chicago, IL 60612, USA. Electronic address: ebongarz@uic.edu.
Mol Ther ; 29(5): 1883-1902, 2021 05 05.
Article in En | MEDLINE | ID: mdl-33508430
Subject(s)
Key words
Fulltext
Add to My VHL
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / White Matter / Galactosylceramidase / Leukodystrophy, Globoid Cell Type of study: Prognostic_studies Limits: Animals Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2021 Document type: Article Affiliation country: Estados Unidos
Fulltext
Add to My VHL
Print
XML
PubMed Links
Search on Google

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / White Matter / Galactosylceramidase / Leukodystrophy, Globoid Cell Type of study: Prognostic_studies Limits: Animals Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2021 Document type: Article Affiliation country: Estados Unidos