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Simoctocog Alfa (Nuwiq) in Previously Untreated Patients with Severe Haemophilia A: Final Results of the NuProtect Study.
Liesner, Ri J; Abraham, Aby; Altisent, Carmen; Belletrutti, Mark J; Carcao, Manuel; Carvalho, Manuela; Chambost, Hervé; Chan, Anthony K C; Dubey, Leonid; Ducore, Jonathan; Gattens, Michael; Gresele, Paolo; Gruel, Yves; Guillet, Benoit; Jimenez-Yuste, Victor; Kitanovski, Lidija; Klukowska, Anna; Lohade, Sunil; Mancuso, Maria Elisa; Oldenburg, Johannes; Pavlova, Anna; Pollio, Berardino; Sigaud, Marianne; Vdovin, Vladimir; Vilchevska, Kateryna; Wu, John K M; Jansen, Martina; Belyanskaya, Larisa; Walter, Olaf; Knaub, Sigurd; Neufeld, Ellis J.
Affiliation
  • Liesner RJ; Great Ormond Street Hospital for Children NHS Trust Haemophilia Centre, NIHR GOSH BRC, London, United Kingdom.
  • Abraham A; Department of Hematology, Christian Medical College, Vellore, India.
  • Altisent C; Unitat d'Hemofilia, Hospital Vall D'Hebron, Barcelona, Spain.
  • Belletrutti MJ; Pediatric Hematology, Department of Pediatrics, University of Alberta, Edmonton, Canada.
  • Carcao M; Division of Haematology/Oncology and Child Health Evaluative Sciences, Department of Paediatrics, Research Institute, Hospital for Sick Children, Toronto, Canada.
  • Carvalho M; Congenital Coagulopathies Reference Centre, São João University Hospital Centre, Porto, Portugal.
  • Chambost H; AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone, Aix Marseille Univ, INSERM, INRA, C2VN, Marseille, France.
  • Chan AKC; Division of Pediatric Hematology/Oncology, McMaster University, Hamilton, Canada.
  • Dubey L; Department of Pediatrics, Western Ukrainian Specialized Children's Medical Centre, Lviv, Ukraine.
  • Ducore J; Department of Pediatrics, University of California Davis Medical Center, Sacramento, United States.
  • Gattens M; Department of Paediatric Haematology and Oncology, Addenbrooke's Hospital, Cambridge University Hospital NHS Foundation Trust, Cambridge, United Kingdom.
  • Gresele P; Department of Medicine and Surgery, University of Perugia, Perugia, Italy.
  • Gruel Y; Centre Régional de Traitement de l'Hémophilie, Hôpital Trousseau, Tours, France.
  • Guillet B; Haemophilia Treatment Centre, Univ Rennes, CHU Rennes, Inserm, EHESP, Irset (Institut de recherche en santé, environnement et travail) - UMR_S 1085, Rennes, France.
  • Jimenez-Yuste V; Servicio de Hematología, Hospital Univeristario La Paz, Autónoma University, Madrid, Spain.
  • Kitanovski L; Department of Haemato-Oncology, University Medical Center Ljubljana, Ljubljana, Slovenia.
  • Klukowska A; Department of Pediatrics, Haematology and Oncology, Warsaw Medical University, Warsaw, Poland.
  • Lohade S; Department of Hematology, Sahyadri Speciality Hospital, Pune, India.
  • Mancuso ME; Center for Thrombosis and Hemorrhagic Diseases, Humanitas Clinical and Research Center - IRCCS, Rozzano, Milan, Italy.
  • Oldenburg J; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Pavlova A; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Pollio B; Department of Transfusion Medicine, Regina Margherita Children Hospital of Turin, Turin, Italy.
  • Sigaud M; Centre Régional de Traitement de I'Hémophilie, University Hospital of Nantes, Nantes, France.
  • Vdovin V; Department of Hematology, Morozovskaya Children's Hospital, Moscow, Russian Federation.
  • Vilchevska K; Department of Hematology, State Institution "Institute of Urgent and Reconstructive Surgery named after V.K. Gusak of National Academy of Medical Sciences of Ukraine," Donetsk, Ukraine.
  • Wu JKM; British Columbia Children's Hospital, Vancouver, Canada.
  • Jansen M; Octapharma Pharmazeutika Produktionsges.mbH, Vienna, Austria.
  • Belyanskaya L; Octapharma AG, Lachen, Switzerland.
  • Walter O; Octapharma AG, Lachen, Switzerland.
  • Knaub S; Octapharma AG, Lachen, Switzerland.
  • Neufeld EJ; St. Jude Children's Research Hospital, Memphis, Tennessee, United States.
Thromb Haemost ; 121(11): 1400-1408, 2021 Nov.
Article in En | MEDLINE | ID: mdl-33581698

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor VIII / Coagulants / Hemophilia A / Hemorrhage / Antibodies Type of study: Clinical_trials / Diagnostic_studies / Observational_studies Limits: Humans / Infant / Male Language: En Journal: Thromb Haemost Year: 2021 Document type: Article Affiliation country: Reino Unido Country of publication: Alemania

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Factor VIII / Coagulants / Hemophilia A / Hemorrhage / Antibodies Type of study: Clinical_trials / Diagnostic_studies / Observational_studies Limits: Humans / Infant / Male Language: En Journal: Thromb Haemost Year: 2021 Document type: Article Affiliation country: Reino Unido Country of publication: Alemania