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Stem Cell Transplantation for Diamond-Blackfan Anemia. A Retrospective Study on Behalf of the Severe Aplastic Anemia Working Party of the European Blood and Marrow Transplantation Group (EBMT).
Miano, Maurizio; Eikema, Dirk-Jan; de la Fuente, Josu; Bosman, Paul; Ghavamzadeh, Ardeshir; Smiers, Frans; Sengeløv, Henrik; Yesilipek, Akif; Formankova, Renata; Bader, Peter; Díaz Pérez, Miguel Ángel; Bertrand, Yves; Niemeyer, Charlotte; Diallo, Safiatou; Ansari, Marc; Bykova, Tatiana A; Faraci, Maura; Bonanomi, Sonia; Gozdzik, Jolanta; Satti, Tariq Mahmood; Bodova, Ivana; Wölfl, Matthias; Rocha, Vanderson G; Mellgren, Karin; Rascon, Jelena; Holter, Wolfgang; Lange, Andrzej; Meisel, Roland; Beguin, Yves; Mozo, Yasmina; Kriván, Gergely; Sirvent, Anne; Bruno, Benedicte; Dalle, Jean Hugues; Onofrillo, Daniela; Giardino, Stefano; Risitano, Antonio M; de Latour, Régis Peffault; Dufour, Carlo.
Affiliation
  • Miano M; Haematology Unit, IRCCS Istituto Giannina Gaslini, Genova, Italy. Electronic address: mauriziomiano@gaslini.org.
  • Eikema DJ; EBMT Statistics, EBMT Data Office, Leiden, Netherlands.
  • de la Fuente J; Centre for Haematology, Imperial College London, London, United Kingdom.
  • Bosman P; EBMT Statistics, EBMT Data Office, Leiden, Netherlands.
  • Ghavamzadeh A; Hematology-Oncology and Stem Cell Transplantation Research Center, Shariati Hospital, Tehran, Iran.
  • Smiers F; Department of Pediatrics, Leiden University Medical Center, Leiden, Netherlands.
  • Sengeløv H; Rigshospitalet Copenhagen, Copenhagen, Denmark.
  • Yesilipek A; Medical Park Antalya Hospital, Antalya, Turkey.
  • Formankova R; University Hospital Motol, Prague, Czech Republic.
  • Bader P; Division for Stem Cell Transplantation and Immunology, Department for Children and Adolescents, University Hospital Frankfurt, Frankfurt, Germany.
  • Díaz Pérez MÁ; Department of Pediatrics, Hematology/Oncology and Hematopoietic Stem Cell Transplant Unit, Hospital Infantil Universitario Niño Jesús, Madrid, Spain.
  • Bertrand Y; Institute of Pediatric Hematology and Oncology, Civil Hospital of Lyon, Lyon, France.
  • Niemeyer C; Division of Pediatric Hematology and Oncology, Department of Pediatrics and Adolescent Medicine, Medical Center, Faculty of Medicine, University of Freiburg, Freiburg, Germany.
  • Diallo S; Department of Hematology, Jules Bordet Institute, Brussels, Belgium.
  • Ansari M; Pediatric Oncology and Hematology, Department of Paediatrics, Gynaecology, and Obstetrics, Geneva University Hospital, Geneva, Switzerland.
  • Bykova TA; Raisa Gorbacheva Memorial Scientific Institute of Children Oncology, Hematology and Transplantation, First Pavlov State Medical University of St. Petersburg, St. Petersburg, Russia.
  • Faraci M; BMT Unit, Istituto Giannina Gaslini, Genova, Italy.
  • Bonanomi S; MBBM Foundation, University of Milano-Bicocca, San Gerardo Hospital, Monza, Italy.
  • Gozdzik J; Jagiellonian University, Medical Collage, Kraków, Poland.
  • Satti TM; Armed Forces Bone Marrow Transplant Centre, Rawalpindi, Pakistan.
  • Bodova I; National Institute of Children's Diseases, Bratislava, Slovakia.
  • Wölfl M; Pediatric Blood and Marrow Transplantation Program, Children's Hospital, University Hospital of Würzburg, Würzburg, Germany.
  • Rocha VG; Churchill Hospital, Oxford, United Kingdom.
  • Mellgren K; Sahlgrenska University Hospital, Gothenburg, Sweden.
  • Rascon J; Center for Pediatric Oncology and Hematology, Vilnius University, Vilnius, Lithuania.
  • Holter W; St. Anna Kinderspital, Vienna, Austria.
  • Lange A; Lower Silesian Center for Cellular Transplantation, Ludwik Hirszfeld Institute of Immunology and Experimental Therapy, Polish Academy of Sciences, Wroclaw, Poland.
  • Meisel R; Division of Pediatric Stem Cell Therapy, Department of Pediatric Oncology, Hematology and Clinical Immunology, Heinrich-Heine-University, Düsseldorf, Germany.
  • Beguin Y; CHU de Liège, University of Liège, Liège, Belgium.
  • Mozo Y; Hospital Universitario La Paz, Madrid, Spain.
  • Kriván G; Department of Paediatric Haematology and Stem Cell Transplantation, Central Hospital of Southern Pest, National Institute of Hematology and Infectious Diseases, Budapest, Hungary.
  • Sirvent A; Onco-Hématologie Pédiatrique, CHU de Montpellier, Montpellier, France.
  • Bruno B; CHU Lille, Hématogie pédiatrique, Lille, France.
  • Dalle JH; Hematology and Immunology Department, Hopital Robert-Debré, Université de Paris, Paris, France.
  • Onofrillo D; Haematology Unit, Ospedale Civile, Pescara, Italy.
  • Giardino S; BMT Unit, Istituto Giannina Gaslini, Genova, Italy.
  • Risitano AM; Department of Clinical Medicine and Surgery, University of Naples, Naples, Italy.
  • de Latour RP; Bone Marrow Transplantation Unit, Saint Louis Hospital, APHP, Paris, France.
  • Dufour C; Haematology Unit, IRCCS Istituto Giannina Gaslini, Genova, Italy.
Transplant Cell Ther ; 27(3): 274.e1-274.e5, 2021 03.
Article in En | MEDLINE | ID: mdl-33781541

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hematopoietic Stem Cell Transplantation / Anemia, Diamond-Blackfan / Anemia, Aplastic Type of study: Observational_studies Limits: Child / Humans Language: En Journal: Transplant Cell Ther Year: 2021 Document type: Article Country of publication: Estados Unidos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Hematopoietic Stem Cell Transplantation / Anemia, Diamond-Blackfan / Anemia, Aplastic Type of study: Observational_studies Limits: Child / Humans Language: En Journal: Transplant Cell Ther Year: 2021 Document type: Article Country of publication: Estados Unidos