Enzyme replacement therapy and hematopoietic stem cell transplant: a new paradigm of treatment in Wolman disease.
Orphanet J Rare Dis
; 16(1): 235, 2021 05 21.
Article
in En
| MEDLINE
| ID: mdl-34020687
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Wolman Disease
/
Hematopoietic Stem Cell Transplantation
/
Enzyme Replacement Therapy
Aspects:
Patient_preference
Limits:
Humans
/
Infant
Language:
En
Journal:
Orphanet J Rare Dis
Journal subject:
MEDICINA
Year:
2021
Document type:
Article
Affiliation country:
Reino Unido
Country of publication:
Reino Unido