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miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3.
Nobre, Rui Jorge; Lobo, Diana D; Henriques, Carina; Duarte, Sonia P; Lopes, Sara M; Silva, Ana C; Lopes, Miguel M; Mariet, Fanny; Schwarz, Lukas K; Baatje, M S; Ferreira, Valerie; Vallès, Astrid; Pereira de Almeida, Luis; Evers, Melvin M; Toonen, Lodewijk J A.
Affiliation
  • Nobre RJ; Center for Neuroscience and Cell Biology (CNC), Molecular Therapy of Brain Disorders Group, University of Coimbra, Coimbra, Portugal.
  • Lobo DD; Center for Innovative Biomedicine and Biotechnology (CIBB), Vectors, Gene and Cell Therapy Group, University of Coimbra, Coimbra, Portugal.
  • Henriques C; ViraVector-Viral Vector for Gene Transfer Core Facility and University of Coimbra, Coimbra, Portugal.
  • Duarte SP; Institute for Interdisciplinary Research (III), University of Coimbra, Coimbra, Portugal.
  • Lopes SM; Center for Neuroscience and Cell Biology (CNC), Molecular Therapy of Brain Disorders Group, University of Coimbra, Coimbra, Portugal.
  • Silva AC; Center for Innovative Biomedicine and Biotechnology (CIBB), Vectors, Gene and Cell Therapy Group, University of Coimbra, Coimbra, Portugal.
  • Lopes MM; Institute for Interdisciplinary Research (III), University of Coimbra, Coimbra, Portugal.
  • Mariet F; Center for Neuroscience and Cell Biology (CNC), Molecular Therapy of Brain Disorders Group, University of Coimbra, Coimbra, Portugal.
  • Schwarz LK; Center for Innovative Biomedicine and Biotechnology (CIBB), Vectors, Gene and Cell Therapy Group, University of Coimbra, Coimbra, Portugal.
  • Baatje MS; ViraVector-Viral Vector for Gene Transfer Core Facility and University of Coimbra, Coimbra, Portugal.
  • Ferreira V; Faculty of Pharmacy, University of Coimbra, Coimbra, Portugal.
  • Vallès A; Center for Neuroscience and Cell Biology (CNC), Molecular Therapy of Brain Disorders Group, University of Coimbra, Coimbra, Portugal.
  • Pereira de Almeida L; Center for Innovative Biomedicine and Biotechnology (CIBB), Vectors, Gene and Cell Therapy Group, University of Coimbra, Coimbra, Portugal.
  • Evers MM; Institute for Interdisciplinary Research (III), University of Coimbra, Coimbra, Portugal.
  • Toonen LJA; Center for Neuroscience and Cell Biology (CNC), Molecular Therapy of Brain Disorders Group, University of Coimbra, Coimbra, Portugal.
Nucleic Acid Ther ; 32(3): 194-205, 2022 06.
Article in En | MEDLINE | ID: mdl-34878314

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Machado-Joseph Disease / MicroRNAs / Ataxin-3 Type of study: Prognostic_studies Limits: Animals Language: En Journal: Nucleic Acid Ther Year: 2022 Document type: Article Affiliation country: Portugal

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Machado-Joseph Disease / MicroRNAs / Ataxin-3 Type of study: Prognostic_studies Limits: Animals Language: En Journal: Nucleic Acid Ther Year: 2022 Document type: Article Affiliation country: Portugal