Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in adults with non-transfusion dependent α-thalassaemia or ß-thalassaemia: an open-label, multicentre, phase 2 study.
Lancet
; 400(10351): 493-501, 2022 08 13.
Article
in En
| MEDLINE
| ID: mdl-35964609
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Piperazines
/
Quinolines
/
Beta-Thalassemia
/
Alpha-Thalassemia
Type of study:
Clinical_trials
/
Prognostic_studies
Limits:
Adult
/
Female
/
Humans
/
Male
/
Middle aged
Language:
En
Journal:
Lancet
Year:
2022
Document type:
Article
Country of publication:
Reino Unido