In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model.
Gene Ther
; 30(5): 443-454, 2023 05.
Article
in En
| MEDLINE
| ID: mdl-36450833
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Amyotrophic Lateral Sclerosis
Limits:
Animals
/
Humans
Language:
En
Journal:
Gene Ther
Journal subject:
GENETICA MEDICA
/
TERAPEUTICA
Year:
2023
Document type:
Article
Affiliation country:
Estados Unidos
Country of publication:
Reino Unido