Correction : Long-term safety and clinical outcomes of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency: two-year results.

Diaz, George A; Giugliani, Roberto; Gufon, Nathalie; Jones, Simon A; Mengel, Eugen; Scarpa, Maurizio; Witters, Peter; Yarramaneni, Abhimanyu; Li, Jing; Armstrong, Nicole M; Kim, Yong; Ortemann-Renon, Catherine; Kumar, Monica

Diaz, George A; Giugliani, Roberto; Gufon, Nathalie; Jones, Simon A; Mengel, Eugen; Scarpa, Maurizio; Witters, Peter; Yarramaneni, Abhimanyu; Li, Jing; Armstrong, Nicole M; Kim, Yong; Ortemann-Renon, Catherine; Kumar, Monica.

Affiliation

Diaz GA; Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, 1 Gustave L. Levy Place, New York, NY, 10029, USA. george.diaz@mssm.edu.
Giugliani R; Medical Genetics Service HCPA, Department of Genetics UFRGS, DASA and Casa Dos Raros, Porto Alegre, Brazil.
Gufon N; Reference Centre of Inherited Metabolic Disease in Femme Mère Enfant Hospital, Hospices Civils of Lyon, Lyon, France.
Jones SA; Manchester University National Health Service Trust, St Mary's Hospital, Manchester, UK.
Mengel E; Institute of Clinical Science for Lysosomal Storage Disorders, SphinCS GmbH, Mainz, Germany.
Scarpa M; University Hospital of Udine, Udine, Italy.
Witters P; University Hospitals Leuven, Louvain, Belgium.
Yarramaneni A; Sanofi, Bridgewater, NJ, USA.
Li J; Sanofi, Bridgewater, NJ, USA.
Armstrong NM; Sanofi, Cambridge, MA, USA.
Kim Y; Sanofi, Paris, France.
Ortemann-Renon C; Sanofi, Bridgewater, NJ, USA.
Kumar M; Sanofi, Bridgewater, NJ, USA.

Orphanet J Rare Dis ; 18(1): 55, 2023 Mar 14.

Article in En | MEDLINE | ID: mdl-36918897

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Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Orphanet J Rare Dis Journal subject: MEDICINA Year: 2023 Document type: Article Affiliation country: Estados Unidos

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