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Advances in therapies for neurological lysosomal storage disorders.
Ellison, S; Parker, H; Bigger, B.
Affiliation
  • Ellison S; Division of Cell Matrix Biology and Regenerative Medicine, University of Manchester, Manchester, United Kingdom.
  • Parker H; Division of Immunology, Immunity to Infection and Respiratory Medicine, University of Manchester, Manchester, United Kingdom.
  • Bigger B; Division of Cell Matrix Biology and Regenerative Medicine, University of Manchester, Manchester, United Kingdom.
J Inherit Metab Dis ; 46(5): 874-905, 2023 09.
Article in En | MEDLINE | ID: mdl-37078180

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Quality of Life / Lysosomal Storage Diseases Aspects: Patient_preference Limits: Child / Humans Language: En Journal: J Inherit Metab Dis Year: 2023 Document type: Article Country of publication: Estados Unidos

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Quality of Life / Lysosomal Storage Diseases Aspects: Patient_preference Limits: Child / Humans Language: En Journal: J Inherit Metab Dis Year: 2023 Document type: Article Country of publication: Estados Unidos