Advances in therapies for neurological lysosomal storage disorders.
J Inherit Metab Dis
; 46(5): 874-905, 2023 09.
Article
in En
| MEDLINE
| ID: mdl-37078180
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Quality of Life
/
Lysosomal Storage Diseases
Aspects:
Patient_preference
Limits:
Child
/
Humans
Language:
En
Journal:
J Inherit Metab Dis
Year:
2023
Document type:
Article
Country of publication:
Estados Unidos