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Real-world evidence of eteplirsen treatment effects in patients with Duchenne muscular dystrophy in the USA.
Iff, Joel; Zhong, Yi; Tuttle, Edward; Gupta, Deepshekhar; Paul, Xander.
Affiliation
  • Iff J; Sarepta Therapeutics, Inc., Cambridge, MA 02142, USA.
  • Zhong Y; Analysis Group, Inc., Menlo Park, CA 94025, USA.
  • Tuttle E; Analysis Group, Inc., Menlo Park, CA 94025, USA.
  • Gupta D; Analysis Group, Inc., Menlo Park, CA 94025, USA.
  • Paul X; Analysis Group, Inc., Menlo Park, CA 94025, USA.
  • Erik Henricson; UC Davis Medical Center, Sacramento, CA 95817, USA.
J Comp Eff Res ; 12(9): e230086, 2023 09.
Article in En | MEDLINE | ID: mdl-37610303

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Dystrophy, Duchenne Type of study: Observational_studies / Risk_factors_studies Limits: Humans Country/Region as subject: America do norte Language: En Journal: J Comp Eff Res Year: 2023 Document type: Article Affiliation country: Estados Unidos Country of publication: Reino Unido

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Dystrophy, Duchenne Type of study: Observational_studies / Risk_factors_studies Limits: Humans Country/Region as subject: America do norte Language: En Journal: J Comp Eff Res Year: 2023 Document type: Article Affiliation country: Estados Unidos Country of publication: Reino Unido