Real-world evidence of eteplirsen treatment effects in patients with Duchenne muscular dystrophy in the USA.
J Comp Eff Res
; 12(9): e230086, 2023 09.
Article
in En
| MEDLINE
| ID: mdl-37610303
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Muscular Dystrophy, Duchenne
Type of study:
Observational_studies
/
Risk_factors_studies
Limits:
Humans
Country/Region as subject:
America do norte
Language:
En
Journal:
J Comp Eff Res
Year:
2023
Document type:
Article
Affiliation country:
Estados Unidos
Country of publication:
Reino Unido