Patient-reported outcomes in Gaucher's disease: a systematic review.
Orphanet J Rare Dis
; 18(1): 244, 2023 08 25.
Article
in En
| MEDLINE
| ID: mdl-37626429
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Lysosomal Storage Diseases
/
Gaucher Disease
Type of study:
Clinical_trials
/
Observational_studies
/
Prevalence_studies
/
Prognostic_studies
/
Qualitative_research
/
Risk_factors_studies
/
Systematic_reviews
Aspects:
Patient_preference
Limits:
Humans
Language:
En
Journal:
Orphanet J Rare Dis
Journal subject:
MEDICINA
Year:
2023
Document type:
Article
Affiliation country:
China