Gene therapy for X-linked myotubular myopathy: the challenges.
Lancet Neurol
; 22(12): 1089-1091, 2023 12.
Article
in En
| MEDLINE
| ID: mdl-37977700
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Myopathies, Structural, Congenital
Limits:
Humans
Language:
En
Journal:
Lancet Neurol
Journal subject:
NEUROLOGIA
Year:
2023
Document type:
Article