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A new age of precision gene therapy.
Schambach, Axel; Buchholz, Christian J; Torres-Ruiz, Raul; Cichutek, Klaus; Morgan, Michael; Trapani, Ivana; Büning, Hildegard.
Affiliation
  • Schambach A; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany; Division of Hematology/Oncology, Boston Children's Hospital, Harvard Medical School, Boston, MA, USA; REBIRTH Research Center for Translational Regenerative Medicine, Hannover Medical School, Hannover, Germany; German
  • Buchholz CJ; Paul-Ehrlich-Institut, Federal Institute for Vaccines and Biomedicines, Langen, Germany; Frankfurt Cancer Institute, Goethe-University, Frankfurt, Germany.
  • Torres-Ruiz R; Division of Hematopoietic Innovative Therapies, Biomedical Innovation Unit, Centro de Investigaciones Energéticas Medioambientales y Tecnológicas and Centro de Investigación Biomédica en Red de Enfermedades Raras, Madrid, Spain; Advanced Therapies Unit, Instituto de Investigación Sanitaria Fundación
  • Cichutek K; Paul-Ehrlich-Institut, Federal Institute for Vaccines and Biomedicines, Langen, Germany.
  • Morgan M; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany.
  • Trapani I; Telethon Institute of Genetics and Medicine, Pozzuoli, Italy; Department of Advanced Biomedical Sciences, Università degli studi di Napoli Federico II, Naples, Italy.
  • Büning H; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany; REBIRTH Research Center for Translational Regenerative Medicine, Hannover Medical School, Hannover, Germany; German Center for Infection Research, partner site Hannover-Braunschweig, Germany. Electronic address: buenin
Lancet ; 403(10426): 568-582, 2024 Feb 10.
Article in En | MEDLINE | ID: mdl-38006899

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: CRISPR-Cas Systems / Gene Editing Limits: Humans Language: En Journal: Lancet Year: 2024 Document type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: CRISPR-Cas Systems / Gene Editing Limits: Humans Language: En Journal: Lancet Year: 2024 Document type: Article