Risdiplam in Spinal Muscular Atrophy: Safety Profile and Use Through The Early Access to Medicine Scheme for the Paediatric Cohort in Great Britain.
J Neuromuscul Dis
; 11(2): 361-368, 2024.
Article
in En
| MEDLINE
| ID: mdl-38189761
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Azo Compounds
/
Muscular Atrophy, Spinal
/
Spinal Muscular Atrophies of Childhood
Type of study:
Prognostic_studies
Limits:
Adolescent
/
Child
/
Child, preschool
/
Humans
/
Infant
/
Newborn
Country/Region as subject:
Europa
Language:
En
Journal:
J Neuromuscul Dis
Year:
2024
Document type:
Article
Country of publication:
Países Bajos