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Onasemnogene Abeparvovec: Post-infusion Efficacy and Safety in Patients With Spinal Muscular Atrophy (SMA)-A Fondazione Policlinico Gemelli IRCCS Experience.
Favia, Michele; Tarantino, Domenico; Cerbo, Lidia Di; Sabia, Antonella; Campopiano, Rina; Pani, Marcello.
Affiliation
  • Favia M; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
  • Tarantino D; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
  • Cerbo LD; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
  • Sabia A; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
  • Campopiano R; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
  • Pani M; Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, Italy.
Hosp Pharm ; 59(1): 39-46, 2024 Feb.
Article in En | MEDLINE | ID: mdl-38223869

Full text: 1 Collection: 01-internacional Database: MEDLINE Type of study: Prognostic_studies Aspects: Patient_preference Language: En Journal: Hosp Pharm Year: 2024 Document type: Article Affiliation country: Italia Country of publication: Estados Unidos

Full text: 1 Collection: 01-internacional Database: MEDLINE Type of study: Prognostic_studies Aspects: Patient_preference Language: En Journal: Hosp Pharm Year: 2024 Document type: Article Affiliation country: Italia Country of publication: Estados Unidos