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Stimulating full-length SMN2 expression by delivering bifunctional RNAs via a viral vector.
Baughan, Travis; Shababi, Monir; Coady, Tristan H; Dickson, Alexa M; Tullis, Gregory E; Lorson, Christian L.
Affiliation
  • Baughan T; Department of Molecular Microbiology and Immunology, Life Sciences Center, University of Missouri, Columbia, MO 65211, USA.
Mol Ther ; 14(1): 54-62, 2006 Jul.
Article in En | MEDLINE | ID: mdl-16580882
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Collection: 01-internacional Database: MEDLINE Main subject: RNA / RNA-Binding Proteins / Cyclic AMP Response Element-Binding Protein / Dependovirus / Genetic Vectors / Nerve Tissue Proteins Type of study: Prognostic_studies Limits: Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2006 Document type: Article Affiliation country: United States Country of publication: United States
Search on Google
Collection: 01-internacional Database: MEDLINE Main subject: RNA / RNA-Binding Proteins / Cyclic AMP Response Element-Binding Protein / Dependovirus / Genetic Vectors / Nerve Tissue Proteins Type of study: Prognostic_studies Limits: Humans Language: En Journal: Mol Ther Journal subject: BIOLOGIA MOLECULAR / TERAPEUTICA Year: 2006 Document type: Article Affiliation country: United States Country of publication: United States