Stimulating full-length SMN2 expression by delivering bifunctional RNAs via a viral vector.
Mol Ther
; 14(1): 54-62, 2006 Jul.
Article
in En
| MEDLINE
| ID: mdl-16580882
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Collection:
01-internacional
Database:
MEDLINE
Main subject:
RNA
/
RNA-Binding Proteins
/
Cyclic AMP Response Element-Binding Protein
/
Dependovirus
/
Genetic Vectors
/
Nerve Tissue Proteins
Type of study:
Prognostic_studies
Limits:
Humans
Language:
En
Journal:
Mol Ther
Journal subject:
BIOLOGIA MOLECULAR
/
TERAPEUTICA
Year:
2006
Document type:
Article
Affiliation country:
United States
Country of publication:
United States