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Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans.
Blood ; 120(18): 3635-46, 2012 Nov 01.
Article in En | MEDLINE | ID: mdl-22968453

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Bone Marrow Transplantation / Severe Combined Immunodeficiency / Hematopoietic Stem Cell Transplantation / Agammaglobulinemia / Genetic Vectors Type of study: Guideline Limits: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Language: En Journal: Blood Year: 2012 Document type: Article Affiliation country: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Genetic Therapy / Bone Marrow Transplantation / Severe Combined Immunodeficiency / Hematopoietic Stem Cell Transplantation / Agammaglobulinemia / Genetic Vectors Type of study: Guideline Limits: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male Language: En Journal: Blood Year: 2012 Document type: Article Affiliation country: United States