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Single-dose, subcutaneous recombinant phenylalanine ammonia lyase conjugated with polyethylene glycol in adult patients with phenylketonuria: an open-label, multicentre, phase 1 dose-escalation trial.
Longo, Nicola; Harding, Cary O; Burton, Barbara K; Grange, Dorothy K; Vockley, Jerry; Wasserstein, Melissa; Rice, Gregory M; Dorenbaum, Alejandro; Neuenburg, Jutta K; Musson, Donald G; Gu, Zhonghua; Sile, Saba.
Affiliation
  • Longo N; University of Utah, Salt Lake City, UT, USA. Electronic address: nicola.longo@hsc.utah.edu.
  • Harding CO; Oregon Health & Sciences University, Portland, OR, USA.
  • Burton BK; Ann and Robert H Lurie Children's Hospital and Northwestern University Feinberg School of Medicine, Chicago, IL, USA.
  • Grange DK; Washington University School of Medicine, St Louis, MO, USA.
  • Vockley J; University of Pittsburgh School of Medicine, PA, USA.
  • Wasserstein M; Mount Sinai School of Medicine, New York, NY, USA.
  • Rice GM; University of Wisconsin, Madison, WI, USA.
  • Dorenbaum A; BioMarin Pharmaceutical, Novato, CA, USA.
  • Neuenburg JK; BioMarin Pharmaceutical, Novato, CA, USA.
  • Musson DG; BioMarin Pharmaceutical, Novato, CA, USA.
  • Gu Z; BioMarin Pharmaceutical, Novato, CA, USA.
  • Sile S; BioMarin Pharmaceutical, Novato, CA, USA.
Lancet ; 384(9937): 37-44, 2014 Jul 05.
Article in En | MEDLINE | ID: mdl-24743000

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Phenylalanine Ammonia-Lyase / Phenylalanine / Phenylketonurias / Polyethylene Glycols Type of study: Clinical_trials Limits: Adult / Female / Humans / Male Country/Region as subject: America do norte Language: En Journal: Lancet Year: 2014 Document type: Article Country of publication: United kingdom

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Phenylalanine Ammonia-Lyase / Phenylalanine / Phenylketonurias / Polyethylene Glycols Type of study: Clinical_trials Limits: Adult / Female / Humans / Male Country/Region as subject: America do norte Language: En Journal: Lancet Year: 2014 Document type: Article Country of publication: United kingdom