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A methodological framework for drug development in rare diseases.
Orphanet J Rare Dis ; 9: 164, 2014 Nov 18.
Article in En | MEDLINE | ID: mdl-25774598

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Orphan Drug Production / Research Design / Clinical Trials as Topic / Rare Diseases Type of study: Clinical_trials / Guideline / Prognostic_studies Aspects: Ethics Limits: Humans Language: En Journal: Orphanet J Rare Dis Journal subject: MEDICINA Year: 2014 Document type: Article Country of publication: United kingdom

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Orphan Drug Production / Research Design / Clinical Trials as Topic / Rare Diseases Type of study: Clinical_trials / Guideline / Prognostic_studies Aspects: Ethics Limits: Humans Language: En Journal: Orphanet J Rare Dis Journal subject: MEDICINA Year: 2014 Document type: Article Country of publication: United kingdom