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Evaluation of 2'-Deoxy-2'-fluoro Antisense Oligonucleotides for Exon Skipping in Duchenne Muscular Dystrophy.
Jirka, Silvana M G; Tanganyika-de Winter, Christa L; Boertje-van der Meulen, Joke W; van Putten, Maaike; Hiller, Monika; Vermue, Rick; de Visser, Peter C; Aartsma-Rus, Annemieke.
Affiliation
  • Jirka SM; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
  • Tanganyika-de Winter CL; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
  • Boertje-van der Meulen JW; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
  • van Putten M; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
  • Hiller M; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
  • Vermue R; BioMarin, Leiden, The Netherlands.
  • de Visser PC; BioMarin, Leiden, The Netherlands.
  • Aartsma-Rus A; Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
Mol Ther Nucleic Acids ; 4: e265, 2015 Dec 01.
Article in En | MEDLINE | ID: mdl-26623937

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Mol Ther Nucleic Acids Year: 2015 Document type: Article Affiliation country: Netherlands Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Mol Ther Nucleic Acids Year: 2015 Document type: Article Affiliation country: Netherlands Country of publication: United States