Your browser doesn't support javascript.
loading
Ambroxol chaperone therapy for neuronopathic Gaucher disease: A pilot study.
Narita, Aya; Shirai, Kentarou; Itamura, Shinji; Matsuda, Atsue; Ishihara, Akiko; Matsushita, Kumi; Fukuda, Chisako; Kubota, Norika; Takayama, Rumiko; Shigematsu, Hideo; Hayashi, Anri; Kumada, Tomohiro; Yuge, Kotaro; Watanabe, Yoriko; Kosugi, Saori; Nishida, Hiroshi; Kimura, Yukiko; Endo, Yusuke; Higaki, Katsumi; Nanba, Eiji; Nishimura, Yoko; Tamasaki, Akiko; Togawa, Masami; Saito, Yoshiaki; Maegaki, Yoshihiro; Ohno, Kousaku; Suzuki, Yoshiyuki.
Affiliation
  • Narita A; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Shirai K; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Itamura S; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Matsuda A; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Ishihara A; Rehabilitation Division Tottori University Hospital Yonago Japan.
  • Matsushita K; Rehabilitation Division Tottori University Hospital Yonago Japan.
  • Fukuda C; Department of Pathobiological Science and Technology Faculty of Medicine Tottori University Yonago Japan.
  • Kubota N; Department of Pediatrics National Hospital Organization Matsue Medical Center Shimane Japan.
  • Takayama R; Department of Pediatrics National Epilepsy Center Shizuoka Institute of Epilepsy and Neurological Disorders Shizuoka Japan.
  • Shigematsu H; Department of Pediatrics National Epilepsy Center Shizuoka Institute of Epilepsy and Neurological Disorders Shizuoka Japan.
  • Hayashi A; Department of Pediatrics Shiga Medical Center for Children Moriyama Japan.
  • Kumada T; Department of Pediatrics Shiga Medical Center for Children Moriyama Japan.
  • Yuge K; Department of Pediatrics and Child Health Kurume University School of Medicine Kurume Japan.
  • Watanabe Y; Department of Pediatrics and Child Health Kurume University School of Medicine Kurume Japan.
  • Kosugi S; Pharmacokinetics and Bioanalysis Center Shin Nippon Biomedical Laboratories, Ltd Kainan Japan.
  • Nishida H; Pharmacokinetics and Bioanalysis Center Shin Nippon Biomedical Laboratories, Ltd Kainan Japan.
  • Kimura Y; Pharmacokinetics and Bioanalysis Center Shin Nippon Biomedical Laboratories, Ltd Kainan Japan.
  • Endo Y; Center for Promoting Next-Generation Highly Advanced Medicine Tottori University Hospital Yonago Japan.
  • Higaki K; Division of Functional Genomics, Research Center for Bioscience and Technology Tottori University Yonago Japan.
  • Nanba E; Division of Functional Genomics, Research Center for Bioscience and Technology Tottori University Yonago Japan.
  • Nishimura Y; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Tamasaki A; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Togawa M; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Saito Y; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Maegaki Y; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Ohno K; Division of Child Neurology Institute of Neurological Science Tottori University Faculty of Medicine Yonago Japan.
  • Suzuki Y; Tokyo Metropolitan Institute of Medical Science Tokyo Japan.
Ann Clin Transl Neurol ; 3(3): 200-15, 2016 Mar.
Article in En | MEDLINE | ID: mdl-27042680

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Ann Clin Transl Neurol Year: 2016 Document type: Article Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Language: En Journal: Ann Clin Transl Neurol Year: 2016 Document type: Article Country of publication: United States