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Activity of daily living for Morquio A syndrome.
Yasuda, Eriko; Suzuki, Yasuyuki; Shimada, Tsutomu; Sawamoto, Kazuki; Mackenzie, William G; Theroux, Mary C; Pizarro, Christian; Xie, Li; Miller, Freeman; Rahman, Tariq; Kecskemethy, Heidi H; Nagao, Kyoko; Morlet, Thierry; Shaffer, Thomas H; Chinen, Yasutsugu; Yabe, Hiromasa; Tanaka, Akemi; Shintaku, Haruo; Orii, Kenji E; Orii, Koji O; Mason, Robert W; Montaño, Adriana M; Fukao, Toshiyuki; Orii, Tadao; Tomatsu, Shunji.
Affiliation
  • Yasuda E; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA; Department of Medical Informatics, Graduate School of Medical Sciences, Kanazawa University, Kanazawa, Japan.
  • Suzuki Y; Department of Hospital Pharmacy, University Hospital, Kanazawa University, Kanazawa, Japan.
  • Shimada T; Medical Education Development Center, Gifu University, Gifu, Japan.
  • Sawamoto K; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Mackenzie WG; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Theroux MC; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Pizarro C; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Xie L; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Miller F; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Rahman T; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Kecskemethy HH; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Nagao K; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Morlet T; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Shaffer TH; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Chinen Y; Department of Pediatrics, Faculty of Medicine, University of the Ryukyus, Ryukyu, Japan.
  • Yabe H; Department of Cell Transplantation and Regenerative Medicine, Tokai University School of Medicine, Isehara, Japan.
  • Tanaka A; Department of Pediatrics, Osaka City University Graduate School of Medicine, Osaka, Japan.
  • Shintaku H; Department of Pediatrics, Osaka City University Graduate School of Medicine, Osaka, Japan.
  • Orii KE; Department of Pediatrics, Graduate School of Medicine, Gifu University, Gifu, Japan.
  • Orii KO; Department of Pediatrics, Graduate School of Medicine, Gifu University, Gifu, Japan.
  • Mason RW; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA.
  • Montaño AM; Department of Pediatrics, Saint Louis University, St. Louis, MO, USA; Department of Biochemistry and Molecular Biology, Saint Louis University, St. Louis, MO, USA.
  • Fukao T; Department of Pediatrics, Graduate School of Medicine, Gifu University, Gifu, Japan.
  • Orii T; Department of Pediatrics, Graduate School of Medicine, Gifu University, Gifu, Japan. Electronic address: orii.tadao@camel.plala.or.jp.
  • Tomatsu S; Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, USA; Department of Pediatrics, Graduate School of Medicine, Gifu University, Gifu, Japan. Electronic address: stomatsu@nemours.org.
Mol Genet Metab ; 118(2): 111-22, 2016 06.
Article in En | MEDLINE | ID: mdl-27161890

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Activities of Daily Living / Mucopolysaccharidosis IV Type of study: Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limits: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant Language: En Journal: Mol Genet Metab Journal subject: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Year: 2016 Document type: Article Affiliation country: Japan Country of publication: United States

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Activities of Daily Living / Mucopolysaccharidosis IV Type of study: Etiology_studies / Incidence_studies / Observational_studies / Risk_factors_studies Limits: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant Language: En Journal: Mol Genet Metab Journal subject: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Year: 2016 Document type: Article Affiliation country: Japan Country of publication: United States