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Long-term exposure to Myozyme results in a decrease of anti-drug antibodies in late-onset Pompe disease patients.
Masat, Elisa; Laforêt, Pascal; De Antonio, Marie; Corre, Guillaume; Perniconi, Barbara; Taouagh, Nadjib; Mariampillai, Kuberaka; Amelin, Damien; Mauhin, Wladimir; Hogrel, Jean-Yves; Caillaud, Catherine; Ronzitti, Giuseppe; Puzzo, Francesco; Kuranda, Klaudia; Colella, Pasqualina; Mallone, Roberto; Benveniste, Olivier; Mingozzi, Federico.
Affiliation
  • Masat E; University Pierre and Marie Curie, INSERM, UMR974, Paris, France.
  • Laforêt P; University Pierre and Marie Curie, INSERM, UMR974, Paris, France.
  • De Antonio M; Paris-Est neuromuscular center, Institute of Myology, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
  • Corre G; University Paris Descartes, INSERM, UMR1138, Paris, France.
  • Perniconi B; Genethon, INSERM, UMR951, Evry, France.
  • Taouagh N; Paris-Est neuromuscular center, Institute of Myology, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
  • Mariampillai K; Paris-Est neuromuscular center, Institute of Myology, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
  • Amelin D; Department of Internal Medicine and Clinical Immunology, DHUI2B, Pitié-Salpêtrière Hospital, AP-HP, Paris, France.
  • Mauhin W; University Pierre and Marie Curie, INSERM, UMR974, Paris, France.
  • Hogrel JY; University Pierre and Marie Curie, INSERM, UMR974, Paris, France.
  • Caillaud C; Neuromuscular Physiology and Evaluation Lab, Institute of Myology, Paris, France.
  • Ronzitti G; Department of Metabolic Biochemistry, Necker Hospital, Paris, France.
  • Puzzo F; Genethon, INSERM, UMR951, Evry, France.
  • Kuranda K; Genethon, INSERM, UMR951, Evry, France.
  • Colella P; University Pierre and Marie Curie, INSERM, UMR974, Paris, France.
  • Mallone R; Genethon, INSERM, UMR951, Evry, France.
  • Benveniste O; Institute Cochin, INSERM U1016, CNRS UMR8104, Paris, France.
  • Mingozzi F; University Paris Descartes, Faculty of Medicine, Paris, France.
Sci Rep ; 6: 36182, 2016 11 04.
Article in En | MEDLINE | ID: mdl-27812025

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease Type II / Alpha-Glucosidases / Enzyme Replacement Therapy / Antibodies Type of study: Observational_studies Limits: Adult / Aged / Female / Humans / Male / Middle aged Language: En Journal: Sci Rep Year: 2016 Document type: Article Affiliation country: France Country of publication: United kingdom

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Glycogen Storage Disease Type II / Alpha-Glucosidases / Enzyme Replacement Therapy / Antibodies Type of study: Observational_studies Limits: Adult / Aged / Female / Humans / Male / Middle aged Language: En Journal: Sci Rep Year: 2016 Document type: Article Affiliation country: France Country of publication: United kingdom