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Stakeholder collaboration for spinal muscular atrophy therapy development.
Aartsma-Rus, Annemieke; Balabanov, Pavel; Binetti, Luca; Haas, Manuel; Haberkamp, Marion; Mitchell, Joanna; Rosa, Mário Miguel; Muntoni, Francesco; Finkel, Richard; Mercuri, Eugenio.
Affiliation
  • Aartsma-Rus A; Leiden University Medical Center, Leiden, Netherlands. Electronic address: a.m.rus@lumc.nl.
  • Balabanov P; European Medicines Agency, Human Medicines Evaluation Division, Scientific and Regulatory Department, Central Nervous System and Ophthalmology Office, London, UK.
  • Binetti L; Famiglie Sma, Milan, Italy.
  • Haas M; European Medicines Agency, Human Medicines Evaluation Division, Scientific and Regulatory Department, Central Nervous System and Ophthalmology Office, London, UK.
  • Haberkamp M; Bundesinstitut für Arzneimittel und Medizinprodukte, 53175 Bonn, Germany.
  • Mitchell J; The SMA Trust, Stratford upon Avon, UK.
  • Rosa MM; Laboratório de Farmacologia Clínica e Terapêutica, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal.
  • Muntoni F; The Dubowitz Neuromuscular Centre, University College London Great Ormond Street Institute of Child Health and Great Ormond Street Hospital, London, UK.
  • Finkel R; Nemours Children's Hospital and University of Central Florida College of Medicine, Orlando, USA.
  • Mercuri E; Catholic University Rome, Italy.
Lancet Neurol ; 16(4): 264, 2017 04.
Article in En | MEDLINE | ID: mdl-28327335

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood Limits: Humans Language: En Journal: Lancet Neurol Journal subject: NEUROLOGIA Year: 2017 Document type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood Limits: Humans Language: En Journal: Lancet Neurol Journal subject: NEUROLOGIA Year: 2017 Document type: Article