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Retrospective observational study of French patients with cystic fibrosis and a Gly551Asp-CFTR mutation after 1 and 2years of treatment with ivacaftor in a real-world setting.
Hubert, Dominique; Dehillotte, Clémence; Munck, Anne; David, Valérie; Baek, Jinmi; Mely, Laurent; Dominique, Stéphane; Ramel, Sophie; Danner Boucher, Isabelle; Lefeuvre, Sylvaine; Reynaud, Quitterie; Colomb-Jung, Virginie; Bakouboula, Prissile; Lemonnier, Lydie.
Affiliation
  • Hubert D; Pulmonary Department, Adult CF Centre, Cochin Hospital, AP-HP, Paris, France; Université Paris Descartes, Sorbonne Paris Cité, Paris, France. Electronic address: dominique.hubert@aphp.fr.
  • Dehillotte C; Vaincre la Mucoviscidose, Paris, France.
  • Munck A; Pediatric CF Centre, Robert Debré Hospital, AP-HP, Paris, France.
  • David V; Pediatric CF Centre, Hôpital Mère-Enfant, Nantes, France.
  • Baek J; Clinical Research Unit, Cochin Hospital, AP-HP, Paris, France.
  • Mely L; CF Centre, Renée Sabran Hospital, Giens, France.
  • Dominique S; Pulmonary Department, Adult CF Centre, Charles Nicolle Hospital, Rouen University Hospital, Rouen, France.
  • Ramel S; CF Centre, Centre héliomarin de Perharidy, Roscoff, France.
  • Danner Boucher I; Pulmonary Department, Adult CF Centre, Laennec Hospital, Nantes, France.
  • Lefeuvre S; Paediatric CF Centre, Hôpital Sud, Rennes, France.
  • Reynaud Q; Adult CF Centre Lyon Sud, Hospices Civils de Lyon, Lyon, France.
  • Colomb-Jung V; Vaincre la Mucoviscidose, Paris, France.
  • Bakouboula P; Clinical Research Unit, Cochin Hospital, AP-HP, Paris, France.
  • Lemonnier L; Vaincre la Mucoviscidose, Paris, France.
J Cyst Fibros ; 17(1): 89-95, 2018 01.
Article in En | MEDLINE | ID: mdl-28711222

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Respiratory System / Quinolones / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Aminophenols / Anti-Bacterial Agents Type of study: Clinical_trials / Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Adolescent / Adult / Child / Female / Humans / Male Country/Region as subject: Europa Language: En Journal: J Cyst Fibros Year: 2018 Document type: Article Country of publication: Netherlands

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Respiratory System / Quinolones / Cystic Fibrosis Transmembrane Conductance Regulator / Cystic Fibrosis / Aminophenols / Anti-Bacterial Agents Type of study: Clinical_trials / Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Adolescent / Adult / Child / Female / Humans / Male Country/Region as subject: Europa Language: En Journal: J Cyst Fibros Year: 2018 Document type: Article Country of publication: Netherlands