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Efficacy of Idebenone to Preserve Respiratory Function above Clinically Meaningful Thresholds for Forced Vital Capacity (FVC) in Patients with Duchenne Muscular Dystrophy.
Mayer, Oscar H; Leinonen, Mika; Rummey, Christian; Meier, Thomas; Buyse, Gunnar M.
Affiliation
  • Mayer OH; The Children's Hospital of Philadelphia, Philadelphia, USA.
  • Leinonen M; Santhera Pharmaceuticals, Liestal, Switzerland.
  • Rummey C; Clinical Data Science, Basel, Switzerland.
  • Meier T; Clinical Data Science, Basel, Switzerland.
  • Buyse GM; Santhera Pharmaceuticals, Liestal, Switzerland.
J Neuromuscul Dis ; 4(3): 189-198, 2017.
Article in En | MEDLINE | ID: mdl-28869486

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Respiration / Vital Capacity / Ubiquinone / Muscular Dystrophy, Duchenne / Antioxidants Type of study: Clinical_trials / Guideline / Prognostic_studies Limits: Adolescent / Child / Humans / Male Language: En Journal: J Neuromuscul Dis Year: 2017 Document type: Article Affiliation country: United States Country of publication: Netherlands

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Respiration / Vital Capacity / Ubiquinone / Muscular Dystrophy, Duchenne / Antioxidants Type of study: Clinical_trials / Guideline / Prognostic_studies Limits: Adolescent / Child / Humans / Male Language: En Journal: J Neuromuscul Dis Year: 2017 Document type: Article Affiliation country: United States Country of publication: Netherlands